Pioneering First Gene Therapy Trial Opens the Door for Reversing Some Previously Incurable Forms of Blindness


Very promising first gene therapy trial opens the door for reversing some previously incurable forms

The sight of thousands of people with previously incurable forms of blindness could be saved thanks to a pioneering new gene therapy that requires just one operation.

In what scientists called a “very promising” first trial, six patients have been successfully treated for choroideremia – an inherited disease that leads to a gradual loss of sight and eventually total blindness.

Charlie Cooper,, ,